The 6-minute walk test and other clinical endpoints in duchenne muscular dystrophy: reliability, concurrent validity, and minimal clinically important differences from a multicenter study.

• An international clinical trial enrolled 174 ambulatory males ≥5 years old with nonsense mutation Duchenne muscular dystrophy (nmDMD). Pretreatment data provide insight into reliability, concurrent validity, and minimal clinically important differences (MCIDs) of the 6-minute walk test (6MWT) and other endpoints.

Ämnesord

MEDICIN OCH HÄLSOVETENSKAP  -- Annan medicin och hälsovetenskap (hsv//swe)

MEDICAL AND HEALTH SCIENCES  -- Other Medical and Health Sciences (hsv//eng)

Nyckelord

Disease Progression

Exercise Test

Heart Rate

drug effects

physiology

Humans

Male

Muscular Dystrophy

Duchenne

diagnosis

drug therapy

physiopathology

Outcome Assessment (Health Care)

Oxadiazoles

therapeutic use

Reproducibility of Results

Time Factors

Walking

physiology

Publikations- och innehållstyp

ref (ämneskategori)

art (ämneskategori)